| 发明名称 |
GENE REPAIR INVOLVING IN VIVO EXCISION OF TARGETING DNA |
| 摘要 |
Methods of modifying, repairing, attenuating and inactivating a gene or other chromosomal DNA in a cell are disclosed. Also disclosed are methods of treating or prophylaxis of a genetic disease in an individual in need thereof.
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| 申请公布号 |
US2012165400(A1) |
申请公布日期 |
2012.06.28 |
| 申请号 |
US201113101463 |
申请日期 |
2011.05.05 |
| 申请人 |
CHOULIKA ANDRE;MULLIGAN RICHARD C.;THE CHILDREN'S MEDICAL CENTER CORPORATION;THE INSTITUTE PASTEUR |
发明人 |
CHOULIKA ANDRE;MULLIGAN RICHARD C. |
| 分类号 |
A61K31/713;C12N15/09;A61K31/711;A61K35/76;A61K48/00;A61P43/00;C12N5/10;C12N15/90 |
主分类号 |
A61K31/713 |
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