| 发明名称 |
DISABLING AUTOPHAGY AS A TREATMENT FOR LYSOSOMAL STORAGE DISEASES |
| 摘要 |
Provided herein are methods of treating lysosomal storage disease, for instance Pompe disease, through inhibition of autophagy. Optionally, treatment is administered as an adjunct to enzyme replacement therapy (ERT).
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| 申请公布号 |
US2012149760(A1) |
申请公布日期 |
2012.06.14 |
| 申请号 |
US201013391265 |
申请日期 |
2010.09.02 |
| 申请人 |
RABEN NINA N.;SCHREINER CYNTHIA;BAUM REBECCA;TAKIKITA SHOICHI;XIE TAO;PLOTZ PAUL H. |
发明人 |
RABEN NINA N.;SCHREINER CYNTHIA;BAUM REBECCA;TAKIKITA SHOICHI;XIE TAO;PLOTZ PAUL H. |
| 分类号 |
A61K31/7088;A61K31/675;A61P3/00 |
主分类号 |
A61K31/7088 |
| 代理机构 |
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