发明名称 Organic Compositions to Treat Beta-ENaC-Related Diseases
摘要 The present disclosure relates to RNAi agents useful in methods of treating Beta-ENaC-related diseases such as cystic fibrosis, pseudohypoaldosteronism type 1 (PHA1), Liddle's syndrome, hypertension, alkalosis, hypokalemia, and obesity-associated hypertension, using a therapeutically effective amount of a RNAi agent to Beta-ENaC.
申请公布号 US2012115934(A1) 申请公布日期 2012.05.10
申请号 US201213355930 申请日期 2012.01.23
申请人 DE FOUGEROLLES ANTONIN;DIENER JOHN L.;HICKMAN EMMA;HINKLE GREGORY;MILSTEIN STUART;PULICHINO ANNE-MARIE;SPRAGUE ANDREW;NOVARTIS AG 发明人 DE FOUGEROLLES ANTONIN;DIENER JOHN L.;HICKMAN EMMA;HINKLE GREGORY;MILSTEIN STUART;PULICHINO ANNE-MARIE;SPRAGUE ANDREW
分类号 A61K31/713;A61P3/00;A61P7/00;A61P9/12;A61P13/12;C07H21/02;C07K14/00;C07K14/79 主分类号 A61K31/713
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