| 发明名称 |
DOMINANT NEGATIVE MUTANTS OF SAM68 FOR USE IN THE TREATMENT OF SPINAL MUSCULAR ATROPHY (SMA) |
| 摘要 |
The present invention relates to the use of dominant negative mutants of Sam68 for the manufacture of a medicament for the treatment of spinal muscular atrophy, to nucleic acids coding for such mutants and to vectors and methods related thereto. |
| 申请公布号 |
US2012071415(A1) |
申请公布日期 |
2012.03.22 |
| 申请号 |
US201013145629 |
申请日期 |
2010.01.20 |
| 申请人 |
PARONETTO MARIA PAOLA;PEDROTTI SIMONA;FONDAZIONE SANTA LUCIA |
发明人 |
PARONETTO MARIA PAOLA;PEDROTTI SIMONA |
| 分类号 |
A61K38/17;A61K48/00;A61P21/00;A61P25/00;C07K14/47;C12N15/63 |
主分类号 |
A61K38/17 |
| 代理机构 |
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代理人 |
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| 主权项 |
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| 地址 |
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