发明名称 Methods for Treating Lysosomal Acid Lipase Deficiency in Patients
摘要 The present invention provides methods of treating LAL deficiency comprising administering to a mammal a therapeutically effective amount of lysosomal acid lipase with an effective dosage frequency. Methods of improving growth and liver function, increasing LAL tissue concentration, and increasing LAL activity in a human patient suffering from LAL deficiency are also provided.
申请公布号 US2012064055(A1) 申请公布日期 2012.03.15
申请号 US201113229558 申请日期 2011.09.09
申请人 QUINN ANTHONY;SYNAGEVA BIOPHARMA CORP. 发明人 QUINN ANTHONY
分类号 A61K38/46;A61P1/16 主分类号 A61K38/46
代理机构 代理人
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