发明名称 TREATMENT OF DYSTROPHIN FAMILY RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO DMD FAMILY
摘要 <p>The present invention relates to antisense oligonucleotides that modulate the expression of and/or function of Dystrophin family, in particular, by targeting natural antisense polynucleotides of Dystrophin family. The invention also relates to the identification of these antisense oligonucleotides and their use in treating diseases and disorders associated with the expression of DMD family.</p>
申请公布号 EP2427554(A2) 申请公布日期 2012.03.14
申请号 EP20100772879 申请日期 2010.05.07
申请人 OPKO CURNA, LLC 发明人 COLLARD, JOSEPH;KHORKOVA SHERMAN, OLGA
分类号 C12N15/113;A61K31/713;A61K48/00;C12N15/63 主分类号 C12N15/113
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