The invention provides optimized miRNA sequences and their therapeutic use. The invention provides optimized miRNA constructs for treatment of neurodegenerative diseases.
申请公布号
WO2012027558(A2)
申请公布日期
2012.03.01
申请号
WO2011US49126
申请日期
2011.08.25
申请人
THE TRUSTEES OF COLUMBIA UNIVERSITY IN THE CITY OF NEW YORK;ABELIOVICH, ASA;RHINN, HERVE;YAMASHITA, TORU