SERCA2 THERAPEUTIC COMPOSITIONS AND METHODS OF USE
摘要
The present invention provides methods for treating pulmonary hypertension in a subject by delivering a therapeutic adeno-associated virus (AAV)-SERCA2 composition to a subject in need thereof.
申请公布号
WO2011130552(A9)
申请公布日期
2012.02.02
申请号
WO2011US32551
申请日期
2011.04.14
申请人
CELLADON CORPORATION;MOUNT SINAI SCHOOL OF MEDICINE;HAJJAR, ROGER, J.;KAWASE, YOSHIAKI;LADAGE, DENNIS;ZSEBO, KRISZTINA