发明名称 VECTORS AND SEQUENCES FOR THE TREATMENT OF DISEASES
摘要 The present invention provides new sequences, gene constructions, vectors and pharmaceutical compositions for the treatment of diseases and specially, for the treatment of mucopolysaccharidoses.
申请公布号 WO2011154520(A1) 申请公布日期 2011.12.15
申请号 WO2011EP59678 申请日期 2011.06.10
申请人 LABORATORIOS DEL DR. ESTEVE, S. A.;UNIVERSIDAD AUTONOMA DE BARCELONA;BOSCH TUBERT, FATIMA;AYUSO LOPEZ, EDUARD;RUZO MATIAS, ALBERT 发明人 BOSCH TUBERT, FATIMA;AYUSO LOPEZ, EDUARD;RUZO MATIAS, ALBERT
分类号 A61K48/00;C12N9/14;C12N9/16;C12N15/67;C12N15/68;C12N15/864 主分类号 A61K48/00
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