| 发明名称 |
A dominant negative mutants of sam68 for use in the treatment of spinal muscular atrophy (sma) |
| 摘要 |
<p>The present invention relates to the use of dominant negative mutants of Sam68 for the manufacture of a medicament for the treatment of spinal muscular atrophy, to nucleic acids coding for such mutants and to vectors and methods related thereto.</p> |
| 申请公布号 |
EP2384202(A1) |
申请公布日期 |
2011.11.09 |
| 申请号 |
EP20100700751 |
申请日期 |
2010.01.20 |
| 申请人 |
FONDAZIONE SANTA LUCIA |
发明人 |
PARONETTO, MARIA PAOLA;PEDROTTI, SIMONA |
| 分类号 |
A61K48/00;C07K14/47 |
主分类号 |
A61K48/00 |
| 代理机构 |
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代理人 |
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| 主权项 |
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| 地址 |
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