发明名称 MODIFIED OLIGONUCLEOTIDES AS REGULATORS OF GENE EXPRESSION
摘要 The invention relates to a compound of pARNi and a group R, where R is selected from alkyl, cycloalkyl, heterocycloalkyl, aryl and heteroaryl and to the synthesis processes thereof. The invention also relates to pharmaceutical compositions comprising the compounds according to the invention, and to the uses thereof in medicine.
申请公布号 WO2011135141(A1) 申请公布日期 2011.11.03
申请号 WO2011ES70296 申请日期 2011.04.26
申请人 CONSEJO SUPERIOR DE INVESTIGACIONES CIENTIFICAS (CSIC);CIBER-BBN;SOMOZA CALATRAVA, ALVARO;MANNING, BRENDAN;ERITJA CASADELLA, RAMON;TERRAZAS MARTINEZ, MONTSERRAT;OCAMPO, SANDRA MILENA;AVINO ANDRES, ANA;PERALES LOSA, JOSE CARLOS 发明人 SOMOZA CALATRAVA, ALVARO;MANNING, BRENDAN;ERITJA CASADELLA, RAMON;TERRAZAS MARTINEZ, MONTSERRAT;OCAMPO, SANDRA MILENA;PERALES LOSA, JOSE CARLOS
分类号 A61K48/00;A61K47/48;C12N15/87 主分类号 A61K48/00
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