发明名称 |
Transferrin/transferrin receptor-mediated siRNA delivery |
摘要 |
The invention provides interfering RNA molecule-ligand conjugates useful as a delivery system for delivering interfering RNA molecules to a cell in vitro or in vivo. The conjugates comprise a ligand that can bind to a transferrin receptor (TfR). Therapeutic uses for the conjugates are also provided.
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申请公布号 |
US7973019(B1) |
申请公布日期 |
2011.07.05 |
申请号 |
US20080244027 |
申请日期 |
2008.10.02 |
申请人 |
ALCON RESEARCH, LTD. |
发明人 |
CHATTERTON JON E.;CLARK ABBOT F. |
分类号 |
A61K48/00;C07H21/02;C07H21/04;C07K16/00 |
主分类号 |
A61K48/00 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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