发明名称 |
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN |
摘要 |
The invention relates to a double-stranded ribonucleic acid (dsRNA) targeting a transthyretin (TTR) gene, and methods of using the dsRNA to inhibit expression of TTR. |
申请公布号 |
KR20110073592(A) |
申请公布日期 |
2011.06.29 |
申请号 |
KR20117011350 |
申请日期 |
2009.10.20 |
申请人 |
ALNYLAM PHARMACEUTICALS, INC. |
发明人 |
SAH DINAH WEN YEE;HINKLE GREGORY;ALVAREZ RENE;MILSTEIN STUART;CHEN QINGMIN |
分类号 |
C12N15/113;A61K31/713;C07H21/02;C12N15/11 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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