发明名称 ANTISENSE MOLECULES AND METHODS FOR TREATING PATHOLOGIES
摘要 An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 59.
申请公布号 WO2011057350(A1) 申请公布日期 2011.05.19
申请号 WO2010AU01520 申请日期 2010.11.12
申请人 THE UNIVERSITY OF WESTERN AUSTRALIA;WILTON, STEPHEN;FLETCHER, SUE;ADAMS, ABBIE;MELONI, PENNY 发明人 WILTON, STEPHEN;FLETCHER, SUE;ADAMS, ABBIE;MELONI, PENNY
分类号 C12N15/113;A61K31/7088;A61K31/712;A61K48/00;A61P21/00 主分类号 C12N15/113
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