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发明名称
ANTISENSE MOLECULES AND METHODS FOR TREATING PATHOLOGIES
摘要
An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 59.
申请公布号
WO2011057350(A1)
申请公布日期
2011.05.19
申请号
WO2010AU01520
申请日期
2010.11.12
申请人
THE UNIVERSITY OF WESTERN AUSTRALIA;WILTON, STEPHEN;FLETCHER, SUE;ADAMS, ABBIE;MELONI, PENNY
发明人
WILTON, STEPHEN;FLETCHER, SUE;ADAMS, ABBIE;MELONI, PENNY
分类号
C12N15/113;A61K31/7088;A61K31/712;A61K48/00;A61P21/00
主分类号
C12N15/113
代理机构
代理人
主权项
地址
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