发明名称 SELECTIVE INHIBITION OF POLYGLUTAMINE PROTEIN EXPRESSION
摘要 The present invention relates to the selective inhibition of protein expression of CAG repeat-related disease proteins such as Huntington using nucleic acid analogs. Peptide nucleic acids and locked nucleic acids are particularly useful analogs.
申请公布号 EP2317847(A1) 申请公布日期 2011.05.11
申请号 EP20090803468 申请日期 2009.07.28
申请人 THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM 发明人 COREY, DAVID, R.;HU, JIAXIN;MATSUI, MASAYUKI
分类号 A01N43/00;A61K31/70;A61K47/48 主分类号 A01N43/00
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