发明名称 DUAL TARGETING SIRNA AGENTS
摘要 <p>The invention relates to dual targeting siRNA agents targeting a PCSK9 gene and a second gene, and methods of using dual targeting siRN A agents to inhibit expression of PCSK.9 and to treat PCSK.9 related disorders, e.g., hypcrlipidcmia.</p>
申请公布号 WO2011038031(A1) 申请公布日期 2011.03.31
申请号 WO2010US49868 申请日期 2010.09.22
申请人 ALNYLAM PHARMACEUTICALS, INC.;FITZGERALD, KEVIN;BUMCROT, DAVID;SAH, DINAH, WEN-YEE;TOUDJARSKA, IVANKA 发明人 FITZGERALD, KEVIN;BUMCROT, DAVID;SAH, DINAH, WEN-YEE;TOUDJARSKA, IVANKA
分类号 A61K31/713;C07H21/02 主分类号 A61K31/713
代理机构 代理人
主权项
地址