发明名称 ENA nucleic acid drugs modifying splicing in mRNA precursor
摘要 Oligonucleotides having a nucleotide sequence complementary to nucleotide numbers such as 2571-2607, 2578-2592, 2571-2592, 2573-2592, 2578-2596, 2578-2601 or 2575-2592 of the dystrophin cDNA (Gene Bank accession No. NM_004006.1) and therapeutic agents for muscular dystrophy comprising such oligonucleotides.
申请公布号 US7902160(B2) 申请公布日期 2011.03.08
申请号 US20030536258 申请日期 2003.11.21
申请人 NONPROFIT ORGANIZATION TRANSLATIONAL RESEARCH ORGANIZATION OF DUCHENNE MUSCULAR DYSTROPHY;KNC LABORATORIES CO., LTD. 发明人 MATSUO MASAFUMI;TAKESHIMA YASUHIRO;KOIZUMI MAKOTO
分类号 A61K31/70;A61K38/00;A61K48/00;A61P21/04;C07H21/04;C12N15/113 主分类号 A61K31/70
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