| 发明名称 |
ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF |
| 摘要 |
An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 202.
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| 申请公布号 |
US2011015253(A1) |
申请公布日期 |
2011.01.20 |
| 申请号 |
US20100837359 |
申请日期 |
2010.07.15 |
| 申请人 |
THE UNIVERSITY OF WESTERN AUSTRALIA |
发明人 |
WILTON STEPHEN DONALD;FLETCHER SUE;MCCLOREY GRAHAM |
| 分类号 |
A61K48/00;A61P21/00;C07H21/00;C12N15/113 |
主分类号 |
A61K48/00 |
| 代理机构 |
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