发明名称 METHODS FOR PREVENTING AND/OR TREATING LYSOSOMAL STORAGE DISORDERS
摘要 The present invention provides methods for preventing and/or treating lysosomal storage disorders using 5-(fluoromethyl)piperdine-3,4-diol, 5- (chloromethyl)piperdine-3,4-diol, or a pharmaceutically acceptable salt, solvate, or prodrug thereof, or any combination of two or more thereof. In particular, the present invention provides methods for preventing and/or treating Gaucher's disease.
申请公布号 CA2758271(A1) 申请公布日期 2010.10.14
申请号 CA20102758271 申请日期 2010.04.09
申请人 AMICUS THERAPEUTICS, INC. 发明人 BOYD, ROBERT;LEE, GARY
分类号 C12Q1/34;A61K31/445;A61P3/00;C12Q1/02 主分类号 C12Q1/34
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