发明名称 CHEMICAL MOLECULES THAT INHIBIT THE SLICING MECHANISM FOR TREATING DISEASES RESULTING FROM SPLICING ANOMALIES
摘要 The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly.
申请公布号 WO2009087238(A3) 申请公布日期 2010.09.16
申请号 WO2009EP50280 申请日期 2009.01.12
申请人 CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS);INSTITUT CURIE;UNIVERSITE MONTPELLIER 2 SCIENCES ET TECHNIQUES;TAZI, JAMAL;GRIERSON, DAVID;MAHUTEAU-BETZER, FLORENCE;ROUX, PIERRE 发明人 TAZI, JAMAL;GRIERSON, DAVID;MAHUTEAU-BETZER, FLORENCE;ROUX, PIERRE
分类号 C07D401/12;A61K31/444;C07D213/74;C07D401/14 主分类号 C07D401/12
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