| 摘要 |
Compounds of formula (I): wherein R1, L2, R2, L3, R3, L4 and R4 are as defined herein, upregulate endogenous utrophin in predictive screens, and thus, are useful for the treatment or prophylaxis of conditions such as Duchenne muscular dystrophy, Becker muscular dystrophy, and cachexia. |
| 申请人 |
BIOMARIN IGA LIMITED;WYNNE, GRAHAM, MICHAEL;WREN, STEPHEN;VAN WELL, RENATE, MARIA;SCHROER, FRANK;LECCI, CRISTINA;POIGNANT, SEVERINE, DANIELLE;MA, SHUCONG;WILSON, FRANCIS |
发明人 |
WYNNE, GRAHAM, MICHAEL;WREN, STEPHEN;VAN WELL, RENATE, MARIA;SCHROER, FRANK;LECCI, CRISTINA;POIGNANT, SEVERINE, DANIELLE;MA, SHUCONG;WILSON, FRANCIS |
