发明名称 |
ENA nucleic acid drugs modifying splicing in mRNA precursor |
摘要 |
<p>Oligonucleotides having a nucleotide sequence complementary to nucleotide numbers such as 2571-2607, 2578-2592, 2571-2592, 2573-2592, 2578-2596, 2578-2601 or 2575-2592 of the dystrophin cDNA (Gene Bank accession No. NM_004006.1) and therapeutic agents for muscular dystrophy comprising such oligonucleotides.</p> |
申请公布号 |
EP2135948(A2) |
申请公布日期 |
2009.12.23 |
申请号 |
EP20090011130 |
申请日期 |
2003.11.21 |
申请人 |
MATSUO, MASAFUMI;NONPROFIT ORGANIZATION TRANSLATIONAL RESEARCH ORGANIZATION OF DUCHENNE MUSCULAR DYSTROPHY;TAKESHIMA, YASUHIRO;DAIICHI SANKYO COMPANY, LIMITED |
发明人 |
MATSUO, MASAFUMI;TAKESHIMA, YASUHIRO;KOIZUMI, MAKOTO |
分类号 |
A61K31/7088;A61K31/712;A61K31/7125;A61K38/00;A61K48/00;A61P21/04;C07H21/04;C12N15/113 |
主分类号 |
A61K31/7088 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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