发明名称 |
Method of enhancing lysosomal alpha-galactosidase A |
摘要 |
A method of enhancing the activity of lysosomal alpha-Galactosidase A (alpha-Gal A) in mammalian cells and for treatment of Fabry disease by administration of 1-deoxy-galactonojirimycin and related compounds.
|
申请公布号 |
US7622485(B2) |
申请公布日期 |
2009.11.24 |
申请号 |
US20040868133 |
申请日期 |
2004.06.14 |
申请人 |
MOUNT SINAI SCHOOL OF MEDICINE OF NEW YORK UNIVERSITY |
发明人 |
FAN JIAN-QIANG;ISHII SATOSHI |
分类号 |
A61K31/445;A61K31/435;A61K31/4465;A61K31/7008;A61K31/7042;A61K31/7052;A61K31/706;A61P43/00;C07D207/12;C07D211/40;C07D211/46;C07H17/02;C12N9/40 |
主分类号 |
A61K31/445 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|