发明名称 Method of enhancing lysosomal alpha-galactosidase A
摘要 A method of enhancing the activity of lysosomal alpha-Galactosidase A (alpha-Gal A) in mammalian cells and for treatment of Fabry disease by administration of 1-deoxy-galactonojirimycin and related compounds.
申请公布号 US7622485(B2) 申请公布日期 2009.11.24
申请号 US20040868133 申请日期 2004.06.14
申请人 MOUNT SINAI SCHOOL OF MEDICINE OF NEW YORK UNIVERSITY 发明人 FAN JIAN-QIANG;ISHII SATOSHI
分类号 A61K31/445;A61K31/435;A61K31/4465;A61K31/7008;A61K31/7042;A61K31/7052;A61K31/706;A61P43/00;C07D207/12;C07D211/40;C07D211/46;C07H17/02;C12N9/40 主分类号 A61K31/445
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