发明名称 NOVEL SIRNA COMPOUNDS FOR INHIBITING RTP801
摘要 The present invention provides chemically modified siRNA compounds that target RTP801 and pharmaceutical compositions comprising same useful for treating microvascular disorders, eye diseases, hearing impairment, neurodegenerative diseases and disorders, spinal cord injury and respiratory conditions.
申请公布号 CA2718765(A1) 申请公布日期 2009.09.24
申请号 CA20092718765 申请日期 2009.03.17
申请人 QUARK PHARMACEUTICALS, INC. 发明人 FEINSTEIN, ELENA;SKALITER, RAMI;KALINSKI, HAGAR;METT, IGOR
分类号 A61K48/00 主分类号 A61K48/00
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