发明名称 |
CHEMICAL MOLECULES THAT INHIBIT THE SLICING MECHANISM FOR TREATING DISEASES RESULTING FROM SPLICING ANOMALIES |
摘要 |
The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly. |
申请公布号 |
CA2711652(A1) |
申请公布日期 |
2009.07.16 |
申请号 |
CA20092711652 |
申请日期 |
2009.01.12 |
申请人 |
INSTITUT CURIE;UNIVERSITE MONTPELLIER 2 SCIENCES ET TECHNIQUES;CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS) |
发明人 |
TAZI, JAMAL;GRIERSON, DAVID;MAHUTEAU-BETZER, FLORENCE;ROUX, PIERRE |
分类号 |
C07D401/12;A61K31/165;A61K31/415;A61K31/4192;A61K31/4439;A61K31/444;A61K31/472;A61P3/10;A61P7/12;A61P9/10;A61P17/00;A61P25/00;A61P31/18;A61P35/00;C07D213/74;C07D213/81;C07D401/14 |
主分类号 |
C07D401/12 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|