发明名称 CHEMICAL MOLECULES THAT INHIBIT THE SLICING MECHANISM FOR TREATING DISEASES RESULTING FROM SPLICING ANOMALIES
摘要 The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly.
申请公布号 CA2946326(A1) 申请公布日期 2009.07.16
申请号 CA20092946326 申请日期 2009.01.12
申请人 CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS);INSTITUT CURIE;UNIVERSITE DE MONTPELLIER 发明人 TAZI, JAMAL;GRIERSON, DAVID;MAHUTEAU-BETZER, FLORENCE;ROUX, PIERRE
分类号 C07C237/34;A61K31/166;A61K31/4164;A61K31/4192;A61P21/00;A61P31/18;A61P35/00;C07D213/82;C07D233/64;C07D249/06;C07D401/12 主分类号 C07C237/34
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