发明名称 |
CHEMICAL MOLECULES THAT INHIBIT THE SLICING MECHANISM FOR TREATING DISEASES RESULTING FROM SPLICING ANOMALIES |
摘要 |
The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly. |
申请公布号 |
CA2946326(A1) |
申请公布日期 |
2009.07.16 |
申请号 |
CA20092946326 |
申请日期 |
2009.01.12 |
申请人 |
CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS);INSTITUT CURIE;UNIVERSITE DE MONTPELLIER |
发明人 |
TAZI, JAMAL;GRIERSON, DAVID;MAHUTEAU-BETZER, FLORENCE;ROUX, PIERRE |
分类号 |
C07C237/34;A61K31/166;A61K31/4164;A61K31/4192;A61P21/00;A61P31/18;A61P35/00;C07D213/82;C07D233/64;C07D249/06;C07D401/12 |
主分类号 |
C07C237/34 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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