发明名称 SELF-COMPLEMENTARY AAV-MEDIATED DELIVERY OF INTERFERING RNA MOLECULES TO TREAT OR PREVENT OCULAR DISORDERS
摘要 The invention provides methods for delivering interfering RNA molecules to an eye of a patient to treat ocular disorders. In particular, the methods of the invention comprise the use of a self-complementary adeno-associated (scAAV) viral vector that can deliver an interfering RNA molecule to an eye of a patient to inhibit expression of a gene that is associated with an ocular disorder.
申请公布号 US2009087413(A1) 申请公布日期 2009.04.02
申请号 US20080243100 申请日期 2008.10.01
申请人 ALCON RESEARCH, LTD. 发明人 SHEPARD ALLAN R.
分类号 A61K48/00;A61K31/7105;A61K35/76;A61P27/02 主分类号 A61K48/00
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