发明名称 |
RNA INTERFERENCE SUPPRESSION OF NEURODEGENERATIVE DISEASES AND METHODS OF USE THEREOF |
摘要 |
The present invention is directed to RNA interference (RNAi) molecules targeted against a nucleic acid sequence that encodes poly-glutamine repeat diseases, and methods of using these RNAi molecules. |
申请公布号 |
US2009036395(A1) |
申请公布日期 |
2009.02.05 |
申请号 |
US20080111025 |
申请日期 |
2008.04.28 |
申请人 |
DAVIDSON BEVERLY L;MAS MONTEYS ALEJANDRO |
发明人 |
DAVIDSON BEVERLY L.;MAS MONTEYS ALEJANDRO |
分类号 |
A61K48/00;A61P25/14;C12N5/10;C12N15/113;C12N15/12;C12N15/861 |
主分类号 |
A61K48/00 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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