发明名称 METHODS AND COMPOSITIONS FOR TREATING SPINAL MUSCULAR ATROPHY
摘要 <p>This invention provides methods of treating and abrogating spinal muscular atrophy by administering an antioxidant. Additionally, the invention provides a method of protecting the SMN protein by administering an antioxidant.</p>
申请公布号 WO2008150509(A1) 申请公布日期 2008.12.11
申请号 WO2008US06944 申请日期 2008.06.02
申请人 THE TRUSTEES OF THE UNIVERSITY OF PENNSYLVANIA;DREYFUSS, GIDEON;WAN, LILI 发明人 DREYFUSS, GIDEON;WAN, LILI
分类号 A61K38/44;C12N9/02 主分类号 A61K38/44
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