| 发明名称 |
Use of nucleoside compounds for nonsense suppression and the treatment of genetic diseases |
| 摘要 |
The invention encompasses nucleoside compounds, compositions comprising the compounds and methods for treating or preventing diseases associated with nonsense mutations of mRNA by administering these compounds or compositions.
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| 申请公布号 |
US7449570(B2) |
申请公布日期 |
2008.11.11 |
| 申请号 |
US20050048659 |
申请日期 |
2005.01.21 |
| 申请人 |
PTC THERAPEUTICS, INC.;AMGEN INC. |
发明人 |
WILDE RICHARD G.;ALMSTEAD NEIL G.;WELCH ELLEN M.;BECKMANN HOLGER |
| 分类号 |
A61K31/7008;A61K31/7028;C07H5/04;C07H7/06;C07H19/00 |
主分类号 |
A61K31/7008 |
| 代理机构 |
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