发明名称 |
Assays For Diagnosing And Evaluating Treatment Options For Fabry Disease |
摘要 |
Provided are in vitro and in vivo methods for determining whether a patient with Fabry disease will respond to treatment with a specific pharmacological chaperone. |
申请公布号 |
US2008056994(A1) |
申请公布日期 |
2008.03.06 |
申请号 |
US20070749512 |
申请日期 |
2007.05.16 |
申请人 |
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发明人 |
KANESKI CHRISTINE;SHIN SANG-HOON;MURRAY GARY;LUDWIG KARIN;LOCKHART DAVID;CASTELLI JEFF |
分类号 |
A61K49/00;C12Q1/02 |
主分类号 |
A61K49/00 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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