发明名称 |
Expression of zeta negative and zeta positive nucleic acids using a dystrophin gene |
摘要 |
Disclosed is expression of zeta negative and zeta positive nucleic acids or nucleic acid complexes using a dystrophin gene in a process for providing nucleic acid expression in a striated (skeletal or cardiac) muscle cell for the purpose of providing a change to the endogenous properties of the cell for cells affected by muscular dystrophy.
|
申请公布号 |
US2007173465(A9) |
申请公布日期 |
2007.07.26 |
申请号 |
US20030339934 |
申请日期 |
2003.01.10 |
申请人 |
MONAHAN SEAN D;WOLFF JON A;SLATTUM PAUL M;HAGSTROM JAMES E;BUDKER VLADIMIR G;ROZEMA DAVID B |
发明人 |
MONAHAN SEAN D.;WOLFF JON A.;SLATTUM PAUL M.;HAGSTROM JAMES E.;BUDKER VLADIMIR G.;ROZEMA DAVID B. |
分类号 |
A61K48/00;A61F5/00 |
主分类号 |
A61K48/00 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|