发明名称 |
SITE-SPECIFIC MODIFICATION OF THE HUMAN GENOME USING CUSTOM-DESIGNED ZINC FINGER NUCLEASES |
摘要 |
Disclosed herein are chimeric zinc finger endonucleases useful in disrupting and/or replacing at least a portion of a gene of interest (e.g. CFTR, DMPK, CCR5, TYR or ßglobin). |
申请公布号 |
WO2007014181(A3) |
申请公布日期 |
2007.05.31 |
申请号 |
WO2006US28739 |
申请日期 |
2006.07.25 |
申请人 |
JOHNS HOPKINS UNIVERSITY;CHANDRASEGARAN, SRINIVASAN |
发明人 |
CHANDRASEGARAN, SRINIVASAN |
分类号 |
C12N15/62;C12N15/09;C12N15/90;C12Q1/68 |
主分类号 |
C12N15/62 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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