发明名称 MULTIPLE-RNAI EXPRESSION CASSETTES FOR SIMULTANEOUS DELIVERY OF RNAI AGENTS RELATED TO HETEROZYGOTIC EXPRESSION PATTERNS
摘要 <p>The present invention provides compositions and methods suitable for expressing y-x multiple-RNAi agents against an allele or alleles of interest in cells, tissues or organs of interest in vitro and in vivo so as to treat diseases.</p>
申请公布号 WO2006116756(A1) 申请公布日期 2006.11.02
申请号 WO2006US16507 申请日期 2006.04.28
申请人 EVERTSZ, ELISABETH;BENITEC, INC.;BRASHEARS, SARAH, J. 发明人 EVERTSZ, ELISABETH;BRASHEARS, SARAH, J.
分类号 C12N15/11;C07H21/04;A01N43/04;C12N5/00;C12P19/34;C12Q1/68 主分类号 C12N15/11
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