| 发明名称 |
Methods for production of non-disease causing hemoglobin by ex vivo oligonucleotide gene editing of human stem/progenitor cells |
| 摘要 |
Methods are presented for applying ex vivo oligonucleotide gene editing to hematopoietic stem cells and/or progenitor cells to create therapeutically effective amounts of wild-type hemoglobin for treatment of the hemoglobinopathies.
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| 申请公布号 |
US2005025753(A1) |
申请公布日期 |
2005.02.03 |
| 申请号 |
US20040837013 |
申请日期 |
2004.04.30 |
| 申请人 |
HAN WEI;CHOMO MATTHEW J.;WONG MARGARET;FISH BARBARA H.;IRELAND CAROLYN M.;BEHRENS DAVETTE L. |
发明人 |
HAN WEI;CHOMO MATTHEW J.;WONG MARGARET;FISH BARBARA H.;IRELAND CAROLYN M.;BEHRENS DAVETTE L. |
| 分类号 |
A01K67/027;A61K;A61K48/00;C12N15/85;(IPC1-7):A61K48/00 |
主分类号 |
A01K67/027 |
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