发明名称 |
Gene therapy for hemophilia a |
摘要 |
Nucleic acid constructs comprising procoagulant gene sequences under the control of a megakaryocyte-specific promoter are provided. The sequences preferably also comprise a secretory granule sorting domain Also provided are vectors comprising the sequences and methods of gene therapy comprising the use of the various constructs.
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申请公布号 |
US2004192599(A1) |
申请公布日期 |
2004.09.30 |
申请号 |
US20040480887 |
申请日期 |
2004.05.18 |
申请人 |
SCHUH ANDRE C;CONWAY EDWARD M |
发明人 |
SCHUH ANDRE C;CONWAY EDWARD M |
分类号 |
C07K14/745;C07K14/755;(IPC1-7):A61K38/37;A61K48/00;C07H21/04 |
主分类号 |
C07K14/745 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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