发明名称 METHODS OF DOWN REGULATING TARGET GENE EXPRESSION IN VIVO BY INTRODUCTION OF INTERFERING RNA
摘要 Methods and compositions are provided for down regulation of target gene expression in vivo by RNA interference. The methods are useful for target discovery and validation of gene-based drug development, and for treatment of human diseases.
申请公布号 WO2004013310(A2) 申请公布日期 2004.02.12
申请号 WO2003US24587 申请日期 2003.08.06
申请人 INTRADIGM CORPORATION;SCARIA, PUTHUPPARAMPIL, V.;WOODLE, MARTIN, C.;LU, PATRICK, Y.;TANG, QINGQUAN;XU, JUN;XIE, FRANK, Y. 发明人 SCARIA, PUTHUPPARAMPIL, V.;WOODLE, MARTIN, C.;LU, PATRICK, Y.;TANG, QINGQUAN;XU, JUN;XIE, FRANK, Y.
分类号 C12N15/09;A61K9/08;A61K9/10;A61K31/7105;A61K35/76;A61K47/34;A61K47/42;A61K48/00;A61P29/00;A61P31/00;A61P35/00;A61P43/00;C12N15/11 主分类号 C12N15/09
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