发明名称 |
Purified nucleic acid molecule for the expression of a lysosomal enzyme and use thereof for preventing or treating lysosomal storage diseases |
摘要 |
A purified nucleic acid molecule which is capable of expressing a lysosomal enzyme wherein said nucleic acid molecule comprises at least a sequence coding for said lysosomal enzyme and a promoter highly active in the brain inserted upstream from said sequence.
|
申请公布号 |
US2004023218(A1) |
申请公布日期 |
2004.02.05 |
申请号 |
US20020176066 |
申请日期 |
2002.06.21 |
申请人 |
DESMARIS NATHALIE;HEARD JEAN MICHEL |
发明人 |
DESMARIS NATHALIE;HEARD JEAN MICHEL |
分类号 |
A61K48/00;C07H21/04;C12N1/21;C12N9/16;C12N9/24;C12N9/36;(IPC1-7):C12Q1/68;C12N9/12;C12P21/02;C12N15/74 |
主分类号 |
A61K48/00 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|