发明名称 |
Gene repair involving in vivo excision of targeting DNA |
摘要 |
Methods of modifying, repairing, attenuating and inactivating a gene or other chromosomal DNA in a cell are disclosed. Also disclosed are methods of treating or prophylaxis of a genetic disease in an individual in need thereof.
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申请公布号 |
US2003229039(A1) |
申请公布日期 |
2003.12.11 |
申请号 |
US20030336069 |
申请日期 |
2003.01.02 |
申请人 |
THE CHILDREN'S MEDICAL CENTER CORPORATION;INSTITUTE PASTEUR |
发明人 |
CHOULIKA ANDRE;MULLIGAN RICHARD C. |
分类号 |
C12N15/09;A61K31/711;A61K35/76;A61K48/00;A61P43/00;C12N5/10;C12N15/90;(IPC1-7):A61K48/00;C12N15/86 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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