MINI-DYSTROPHIN NUCLEIC ACID AND PEPTIDE SEQUENCES
摘要
The present invention relates to compositions and methods for expressing mini-dystrophin peptides. In particular, the present invention provides compositions comprising nucleic acid sequences that are shorter than wild-type dystrophin cDNA and that express mini-dystrophin peptides that function in a similar manner as wild-type dystrophin proteins. The present invention also provides compositions comprising mini-dystrophin peptides, and methods for expressing mini-dystrophin peptides in target cells.
申请公布号
WO0229056(A3)
申请公布日期
2003.09.18
申请号
WO2001US31126
申请日期
2001.10.04
申请人
REGENTS OF THE UNIVERSITY OF MICHIGAN;CHAMBERLAIN, JEFFREY, S.;HARPER, SCOTT, Q.