发明名称 USE OF RECOMBINANT GENE DELIVERY VECTORS FOR TREATING OR PREVENTING LYSOSOMAL STORAGE DISORDERS
摘要 Gene delivery vectors, such as, for example, recombinant FIV vectors, and methods of using such vectors are provided for use in treating or preventing retinal diseases of the eye and diseases of the brain associated with lysosomal storage disorders.
申请公布号 WO0073482(A9) 申请公布日期 2002.04.18
申请号 WO2000US14582 申请日期 2000.05.26
申请人 CHIRON CORPORATION;UNIVERSITY OF IOWA RESEARCH FOUNDATION;DAVIDSON, BEVERLY, L.;JOLLY, DOUGLAS, J.;SAUTER, SYBILLE, L.;GHODSI, ADBI;STEIN, COLLEEN, S.;DERKSEN, TODD, A.;DUBENSKY, THOMAS, W., JR.;HETH, JASON, A. 发明人 DAVIDSON, BEVERLY, L.;JOLLY, DOUGLAS, J.;SAUTER, SYBILLE, L.;GHODSI, ADBI;STEIN, COLLEEN, S.;DERKSEN, TODD, A.;DUBENSKY, THOMAS, W., JR.;HETH, JASON, A.
分类号 C12N15/09;A61K9/14;A61K35/76;A61K38/46;A61K48/00;A61P25/28;A61P27/02;A61P43/00;C12N5/10;C12N7/00;C12N7/01;C12N9/24;C12N15/54;C12N15/867;(IPC1-7):C12N15/867 主分类号 C12N15/09
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