发明名称 MEDICAL PREPARATIONS FOR THE TREATMENT OF ALPHA-GALACTOSIDASE A DEFICIENCY
摘要 <p>The invention provides highly purified ±-Gal A, and various methods for purifying it; ±-Gal A preparations with altered charge and methods for making those preparations; ±-Gal A preparations that have an extended circulating half-life in a mammalian host, and methods for making same; and methods and dosages for administering an ±-Gal A preparation to a subject.</p>
申请公布号 EP1163349(A2) 申请公布日期 2001.12.19
申请号 EP20000913825 申请日期 2000.03.09
申请人 TRANSKARYOTIC THERAPIES, INC. 发明人 SELDEN, RICHARD, F.;BOROWSKI, MARIANNE;KINOSHITA, CAROL, M.;TRECO, DOUGLAS, A.;WILLIAMS, MELANIE, D.;SCHUETZ, THOMAS, J.;DANIEL, PETER, F.
分类号 A61K38/12;A61K38/00;A61K48/00;C07K14/61;C12N9/24;C12N9/40;C12N15/54;C12N15/56;(IPC1-7):C12N15/56;A61K38/46;C12N15/63;C12P21/02 主分类号 A61K38/12
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