发明名称 Agent for gene therapy of dilated cardomyopathy
摘要 According to the present invention, there is provided a gene expression vector which is obtained by inserting a gene encoding sarcoglycan into an adeno-associated virus (AAV) vector. By administering the gene expression vector of the present invention to a living body in vivo, a sarcoglycan can be continuously expressed in the living body, so that the restoration of alpha, beta, gamma- and delta-sarcoglycan components can be accompanied and the heart function of the patient of dilated cardiomyopathy can be improved.
申请公布号 US2001029040(A1) 申请公布日期 2001.10.11
申请号 US20010768807 申请日期 2001.01.25
申请人 TOYO-OKA TERUHIKO 发明人 TOYO-OKA TERUHIKO
分类号 C12N15/09;A61K31/7088;A61K48/00;A61P9/00;A61P43/00;C07K14/47;(IPC1-7):A61K48/00;C12N7/01 主分类号 C12N15/09
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