发明名称 PHARMACEUTICAL COMPOSITION COMPRISING NO OR AT LEAST A NO DONOR COMPOUND OR ANOTHER COMPOUND CAPABLE OF RELEASING OR INDUCING NO FORMATION IN CELLS
摘要 The invention concerns the use of NO, a NO donor compound or a compound capable or releasing, stimulating or inducing NO formation in cells to prepare a medicine for treating or preventing a disease resulting from deficiency of an adult gene in a person for the re-expression of said homologous foetal gene. The invention particularly concerns the treatment of Duchenne or Becker muscular dystrophy, or thalassemia or sickle cell disease.
申请公布号 WO0076451(A2) 申请公布日期 2000.12.21
申请号 WO2000FR01612 申请日期 2000.06.09
申请人 CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE - CNRS;ISRAEL, MAURICE;DE LA PORTE, SABINE;FOSSIER, PHILIPPE;CHAUBOURT, EMMANUEL;BAUX, GERARD;LEPRINCE, CHRISTIANE 发明人 ISRAEL, MAURICE;DE LA PORTE, SABINE;FOSSIER, PHILIPPE;CHAUBOURT, EMMANUEL;BAUX, GERARD;LEPRINCE, CHRISTIANE
分类号 A61K33/00;A61K31/04;A61K31/198;A61K31/26;A61K31/5377;A61K33/24;A61P7/00;A61P7/06;A61P21/00;A61P21/04;(IPC1-7):A61K/ 主分类号 A61K33/00
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