发明名称 |
GENE REPAIR INVOLVING THE INDUCTION OF DOUBLE-STRANDED DNA CLEAVAGE AT A CHROMOSOMAL TARGET SITE |
摘要 |
Methods of modifying, repairing, attenuating and inactivating a gene or other chromosomal DNA in a cell are disclosed. Also disclosed are methods of treating or prophylaxis of a genetic disease in an individual in need thereof. Further disclosed are chimeric restriction endonucleases. |
申请公布号 |
WO0046386(A2) |
申请公布日期 |
2000.08.10 |
申请号 |
WO2000US03014 |
申请日期 |
2000.02.03 |
申请人 |
THE CHILDREN'S MEDICAL CENTER CORPORATION;THE INSTITUTE PASTEUR;CHOULIKA, ANDRE;MULLIGAN, RICHARD, C. |
发明人 |
CHOULIKA, ANDRE;MULLIGAN, RICHARD, C. |
分类号 |
C12N15/09;A61K31/7088;A61K48/00;A61P43/00;C12N5/10;C12N9/22;C12N15/90 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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