发明名称 |
GENE REPAIR INVOLVING IN VIVO EXCISION OF TARGETING DNA |
摘要 |
Methods of modifying, repairing, attenuating and inactivating a gene or othe r chromosomal DNA in a cell through SCEI-induced recombination are disclosed. Also disclosed are methods of treating or prophylaxis of a genetic disease i n an individual in need thereof.
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申请公布号 |
CA2360878(A1) |
申请公布日期 |
2000.08.10 |
申请号 |
CA20002360878 |
申请日期 |
2000.02.03 |
申请人 |
THE INSTITUTE PASTEUR;THE CHILDREN'S MEDICAL CENTER CORPORATION |
发明人 |
CHOULIKA, ANDRE;MULLIGAN, RICHARD C. |
分类号 |
C12N15/09;A61K31/711;A61K35/76;A61K48/00;A61P43/00;C12N5/10;C12N15/90;(IPC1-7):C12N15/90;C12N9/22 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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