发明名称 |
ANTI-SICKLING BETA-GLOBIN PROTEIN, COMPOSITIONS AND METHODS FOR TREATING SICKLE CELL DISEASE |
摘要 |
<p>Gene therapy methods and compositions for high level expression of anti-sickling globin proteins in erythroid cells for treating Sickle Cell disease are described.</p> |
申请公布号 |
GR3031229(T3) |
申请公布日期 |
1999.12.31 |
申请号 |
GR19990402320T |
申请日期 |
1999.09.16 |
申请人 |
MASSACHUSETTS INSTITUTE OF TECHNOLOGY |
发明人 |
LEBOULCH, PHILIPPE;LONDON, IRVING, M. |
分类号 |
C12N15/09;A61K35/76;A61K38/00;A61K38/16;A61K48/00;A61P7/00;C07K14/805;C12N5/10;C12N15/12;C12P21/02;(IPC1-7):C12N15/12;A61K38/42;C12N15/86 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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