发明名称 METHOD FOR RECOMBINANT ADENO-ASSOCIATED VIRUS-DIRECTED GENE THERAPY
摘要 A method of prolonging gene expression by reducing immune response to a recombinant adeno-associated virus (AAV) bearing a desired gene administered into the muscle of a mammal is described.
申请公布号 WO9809657(A2) 申请公布日期 1998.03.12
申请号 WO1997US15692 申请日期 1997.09.04
申请人 TRUSTEES OF THE UNIVERSITY OF PENNSYLVANIA;WILSON, JAMES, M.;FISHER, KRISHNA, J. 发明人 WILSON, JAMES, M.;FISHER, KRISHNA, J.
分类号 A61K48/00;A61K35/76;A61K38/00;A61K38/21;A61K38/22;A61K38/27;A61K38/28;A61K38/43;C12N15/864 主分类号 A61K48/00
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