METHOD FOR RECOMBINANT ADENO-ASSOCIATED VIRUS-DIRECTED GENE THERAPY
摘要
A method of prolonging gene expression by reducing immune response to a recombinant adeno-associated virus (AAV) bearing a desired gene administered into the muscle of a mammal is described.
申请公布号
WO9809657(A2)
申请公布日期
1998.03.12
申请号
WO1997US15692
申请日期
1997.09.04
申请人
TRUSTEES OF THE UNIVERSITY OF PENNSYLVANIA;WILSON, JAMES, M.;FISHER, KRISHNA, J.