| 发明名称 |
AMINOGLYCOSIDES AND USES THEREOF IN TREATING GENETIC DISORDERS |
| 摘要 |
PROBLEM TO BE SOLVED: To provide novel aminoglycosides that increase the expression level of a gene having a premature stop-codon mutation and have improved effect in the treatment of genetic disorders such as Duchenne muscular dystrophy and hemophilia.SOLUTION: The present invention provides aminoglycoside compounds illustrated by the following formulas.SELECTED DRAWING: None |
| 申请公布号 |
JP2016121168(A) |
申请公布日期 |
2016.07.07 |
| 申请号 |
JP20160011038 |
申请日期 |
2016.01.22 |
| 申请人 |
TECHNION RESEARCH & DEVELOPMENT FOUNDATION LTD |
发明人 |
TIMOR BAASOV;DANA ATIA-GLIKIN;JEYAKUMAR KANDASAMY;VALERY BELAKHOV |
| 分类号 |
C07H15/23;A61K31/7036;A61P7/04;A61P13/12;A61P21/00;A61P21/04;A61P43/00;C12N15/09 |
主分类号 |
C07H15/23 |
| 代理机构 |
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