发明名称 COMPOSITIONS AND METHODS FOR TREATMENT OF MUSCULAR DYSTROPHY
摘要 The present invention features recombinant adeno-associated vectors for delivery of genes to both skeletal and cardiac muscle and methods for treatment of muscle defects, including Duchenne's muscular dystrophy.
申请公布号 US2016303255(A1) 申请公布日期 2016.10.20
申请号 US201414909854 申请日期 2014.07.26
申请人 CONSIGLIO NAZIONALE DELLE RICERCHE 发明人 PASSANANTI Claudio;CORBI Nicoletta;DI CERTO Maria Grazia;MATTEI Elisabetta;PISANI Cinzia;STRIMPAKOS Georgios
分类号 A61K48/00;C07K14/47;C12N15/86;C07K14/005 主分类号 A61K48/00
代理机构 代理人
主权项
地址 Roma IT