发明名称 |
COMPOSITIONS AND METHODS FOR TREATMENT OF MUSCULAR DYSTROPHY |
摘要 |
The present invention features recombinant adeno-associated vectors for delivery of genes to both skeletal and cardiac muscle and methods for treatment of muscle defects, including Duchenne's muscular dystrophy. |
申请公布号 |
US2016303255(A1) |
申请公布日期 |
2016.10.20 |
申请号 |
US201414909854 |
申请日期 |
2014.07.26 |
申请人 |
CONSIGLIO NAZIONALE DELLE RICERCHE |
发明人 |
PASSANANTI Claudio;CORBI Nicoletta;DI CERTO Maria Grazia;MATTEI Elisabetta;PISANI Cinzia;STRIMPAKOS Georgios |
分类号 |
A61K48/00;C07K14/47;C12N15/86;C07K14/005 |
主分类号 |
A61K48/00 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
Roma IT |